Paulo Fontoura

Paulo Fontoura

Company: Roche

Job title: Global Head & SVP, Neuroscience & Rare Diseases Clinical Development

Seminars:

Live Q&A 3:05 pm

Read more

day: Day One

Discovering an Innovative Approach to Trial Design for Real World SMA Population 1:50 pm

• Designing a clinical development program across a range of ages and disabilities • Evaluating whether SMN protein or other blood biomarker levels associate with improved motor function in SMA patients and using these to monitor or predict treatment outcomes • Determining the right dose based on the biomarker, pivot from dose ranging safety portion…Read more

day: Day One

Kick-Off Panel Discussion: Dissecting Fundamental Questions Arising for Each Therapeutic Approach 9:05 am

• A critical overview of the current status of knowledge and therapies for neuromuscular disorders, focusing on ALS, SMA and DMD • What have we unravelled over the last year that will drive more effective clinical development to reach patients in need? • What are the unique challenges for ASO therapy, gene therapy, gene modification…Read more

day: Day One

© Copyright 2018 Hanson Wade | Design and site by Event Engine | Hanson Wade Limited is registered in England & Wales, number 06752216.
Registered Office: Suite A, 6 Honduras Street, London EC1Y 0TH.