Content Library

2019 Presentations

Moving to Restore Muscle Function in Addition to Slowing Progression

Kenneth Attie, Acceleron Pharma

Duchenne Regulatory Science Consortium (DRSC) Clinical Trial Simulation Tool

Jane Larkindale, Critical Path Institute

Small Molecule Fast Skeletal Muscle Troponin Activators
as Potential Therapeutics for Neuromuscular Diseases

Darren Hwee, Cytokinetics

Focused Evolution of CNS-targeting
AAV Vectors Using Cell Type-
Specific RNA Expression

Mathieu Nonnenmacher, Voyager Therapeutics